A single gene therapy using patients' own stem cells has cured 95 percent of treated children with a deadly immune disorder. The treatment uses the patient's own stem cells that are genetically modified to produce the missing enzyme.
Scientists have created a new version of CRISPR gene editing that makes 60 times fewer errors than before.
The study shows that patients who received high doses had fewer symptoms and produced 8.2 percent less of a protein that indicates dying nerve cells.
Researchers have discovered genes that control how large tomatoes and eggplants can grow. New techniques in gene editing can lead to the development of new varieties of traditional tomatoes and eggplants that are both larger and tastier.
Genetic researcher Beth Shapiro leads the work to recreate the dodo, a bird that went extinct over 300 years ago. The technology being developed can be used to save currently endangered species, like the pink pigeon in Mauritius.
A child with a deadly metabolic disease has been successfully treated with a new type of gene editing called ARCUS. The treatment allowed the child to stop their special diet after three months.
Researchers at Arc Institute have discovered a completely new molecular system for editing DNA using RNA. The system enables programmable DNA changes such as inserting, removing or inverting DNA sequences.
The treatment involved a 16-minute operation where she received a functional copy of a gene that is crucial for hearing. The gene has made her hearing almost completely restored. Opal Sandy can now hear sounds as soft as a whisper.
Scientists have used CRISPR technology to create tomatoes that use water more efficiently. These tomatoes require less water to grow but still produce the same amount of tomatoes, with the same taste and quality.