A nine and a half month old boy received the world's first custom gene editing treatment for his rare genetic disease CPS1 deficiency. The treatment fixed the boy's specific mutation and he can now eat normal amounts of protein without getting dangerous ammonia levels in his blood.
Researchers have discovered genes that control how large tomatoes and eggplants can grow. New techniques in gene editing can lead to the development of new varieties of traditional tomatoes and eggplants that are both larger and tastier.
Hell will break loose, said a Nobel Prize winner. We will see baby factories, said others. That's how they talked about in vitro fertilization then. We can learn from that now.
The first treatment using CRISPR technology has begun being administered to patients with sickle cell disease and beta-thalassemia. Patients do not produce healthy hemoglobin. Casgevy uses CRISPR to modify the patient's own cells so they produce healthy hemoglobin.
The OpenCRISPR initiative aims to democratize gene technology and accelerate the development of customized genetic treatments. By making this technology available, Profluent hopes to increase access and reduce the costs of gene editing treatments.
Scientists have used CRISPR technology to create tomatoes that use water more efficiently. These tomatoes require less water to grow but still produce the same amount of tomatoes, with the same taste and quality.
For the first time, surgeons have transplanted a kidney from a genetically modified pig into a living person. This type of kidney could help reduce the shortage of organs.
The FDA recently approved a pioneering CRISPRβCas9 therapy for sickle cell disease, marking a historic moment in genetic treatment. But that it is just the tip of the iceberg.
The approvals include the first-ever CRISPR-Cas9 based drug, Casgevy, and a gene therapy drug, Lyfgenia, marking a milestone in medical biotechnology.